Entry - #613500 - AGAMMAGLOBULINEMIA 2, AUTOSOMAL RECESSIVE; AGM2 - OMIM - (MIRROR)
# 613500

AGAMMAGLOBULINEMIA 2, AUTOSOMAL RECESSIVE; AGM2


Alternative titles; symbols

AGAMMAGLOBULINEMIA, AUTOSOMAL RECESSIVE, DUE TO IGLL1 DEFECT


Phenotype-Gene Relationships

Location Phenotype Phenotype
MIM number
Inheritance Phenotype
mapping key
Gene/Locus Gene/Locus
MIM number
22q11.23 Agammaglobulinemia 2 613500 AR 3 IGLL1 146770
Clinical Synopsis
 
Phenotypic Series
 

INHERITANCE
- Autosomal recessive
HEAD & NECK
Ears
- Otitis, recurrent
RESPIRATORY
- Recurrent respiratory infections
Lung
- Pneumonia, recurrent
NEUROLOGIC
Central Nervous System
- Meningitis
IMMUNOLOGY
- Recurrent bacterial infections
- Absent or severely reduced numbers of B cells
- Inability to mount antibody response to antigen
- Normal numbers and function of T cells
- Hypogammaglobulinemia, profound
- Agammaglobulinemia
MISCELLANEOUS
- One family has been reported (last curated May 2013)
- Onset in infancy
MOLECULAR BASIS
- Caused by mutation in the immunoglobulin lambda-like polypeptide 1 gene (IGLL1, 146770.0001)

TEXT

A number sign (#) is used with this entry because of evidence that this form of autosomal recessive agammaglobulinemia, referred to here as agammaglobulinemia-2 (AGM2), is caused by homozygous or compound heterozygous mutation in the immunoglobulin lambda-like-1 gene (IGLL1; 146770) on chromosome 22q11.

For a general phenotypic description and a discussion of genetic heterogeneity of autosomal agammaglobulinemia, see AGM1 (601495).


Clinical Features

Minegishi et al. (1998) reported a boy with agammaglobulinemia and markedly reduced numbers of B cells. He had onset of recurrent otitis at 2 months of age and was found to have hypogammaglobulinemia and absent B cells at 3 years of age when he developed Haemophilus meningitis complicated by arthritis. Laboratory studies at that time showed he was seronegative for the T cell-dependent antigens tetanus toxoid, diphtheria toxoid, and conjugated Haemophilus influenzae, despite previous immunization. He also failed to make antibody to the T cell-independent antigens in blood group substances. He had never had detectable CD19+ B cells by routine clinical testing. At 5 years of age, while receiving gammaglobulin replacement therapy, he had no measurable serum IgM and IgA. However, he had normal numbers of T cells and normal proliferative responses to mitogens.


Inheritance

The transmission pattern of AGM2 in the family reported by Minegishi et al. (1998) was consistent with autosomal recessive inheritance.


Molecular Genetics

In a boy with agammaglobulinemia and markedly reduced numbers of B cells, Minegishi et al. (1998) identified compound heterozygosity for 2 mutations in the IGLL1 gene (146770.0001; 146770.0002). Each healthy parent was heterozygous for one of the mutations.

In 2 sisters (EGS539 and EGS540) with B-cell deficiency and increased susceptibility to bacterial infections, Moens et al. (2014) identified a homozygous 1-bp deletion (c.258delG; 146770.0003) in the IGLL1 gene. No additional clinical details were provided.


REFERENCES

  1. Minegishi, Y., Coustan-Smith, E., Wang, Y.-H., Cooper, M. D., Campana, D., Conley, M. E. Mutations in the human lambda-5/14.1 gene result in B cell deficiency and agammaglobulinemia. J. Exp. Med. 187: 71-77, 1998. [PubMed: 9419212, images, related citations] [Full Text]

  2. Moens, L. N., Falk-Sorqvist, E., Asplund, A. C., Bernatowska, E., Smith, C. I. E., Nilsson, M. Diagnostics of primary immunodeficiency diseases: a sequencing capture approach. PLoS One 9: e114901, 2014. Note: Electronic Article. [PubMed: 25502423, related citations] [Full Text]


Joanna S. Amberger - updated : 06/13/2016
Joanna S. Amberger - updated : 8/14/2015
Creation Date:
Cassandra L. Kniffin : 7/26/2010
alopez : 11/15/2022
carol : 06/08/2020
carol : 06/13/2016
joanna : 8/14/2015
carol : 5/1/2013
ckniffin : 5/1/2013
terry : 4/28/2011
terry : 4/27/2011
carol : 8/3/2010
ckniffin : 7/29/2010

# 613500

AGAMMAGLOBULINEMIA 2, AUTOSOMAL RECESSIVE; AGM2


Alternative titles; symbols

AGAMMAGLOBULINEMIA, AUTOSOMAL RECESSIVE, DUE TO IGLL1 DEFECT


ORPHA: 229717, 33110;   DO: 0081135;  


Phenotype-Gene Relationships

Location Phenotype Phenotype
MIM number
Inheritance Phenotype
mapping key
Gene/Locus Gene/Locus
MIM number
22q11.23 Agammaglobulinemia 2 613500 Autosomal recessive 3 IGLL1 146770

TEXT

A number sign (#) is used with this entry because of evidence that this form of autosomal recessive agammaglobulinemia, referred to here as agammaglobulinemia-2 (AGM2), is caused by homozygous or compound heterozygous mutation in the immunoglobulin lambda-like-1 gene (IGLL1; 146770) on chromosome 22q11.

For a general phenotypic description and a discussion of genetic heterogeneity of autosomal agammaglobulinemia, see AGM1 (601495).


Clinical Features

Minegishi et al. (1998) reported a boy with agammaglobulinemia and markedly reduced numbers of B cells. He had onset of recurrent otitis at 2 months of age and was found to have hypogammaglobulinemia and absent B cells at 3 years of age when he developed Haemophilus meningitis complicated by arthritis. Laboratory studies at that time showed he was seronegative for the T cell-dependent antigens tetanus toxoid, diphtheria toxoid, and conjugated Haemophilus influenzae, despite previous immunization. He also failed to make antibody to the T cell-independent antigens in blood group substances. He had never had detectable CD19+ B cells by routine clinical testing. At 5 years of age, while receiving gammaglobulin replacement therapy, he had no measurable serum IgM and IgA. However, he had normal numbers of T cells and normal proliferative responses to mitogens.


Inheritance

The transmission pattern of AGM2 in the family reported by Minegishi et al. (1998) was consistent with autosomal recessive inheritance.


Molecular Genetics

In a boy with agammaglobulinemia and markedly reduced numbers of B cells, Minegishi et al. (1998) identified compound heterozygosity for 2 mutations in the IGLL1 gene (146770.0001; 146770.0002). Each healthy parent was heterozygous for one of the mutations.

In 2 sisters (EGS539 and EGS540) with B-cell deficiency and increased susceptibility to bacterial infections, Moens et al. (2014) identified a homozygous 1-bp deletion (c.258delG; 146770.0003) in the IGLL1 gene. No additional clinical details were provided.


REFERENCES

  1. Minegishi, Y., Coustan-Smith, E., Wang, Y.-H., Cooper, M. D., Campana, D., Conley, M. E. Mutations in the human lambda-5/14.1 gene result in B cell deficiency and agammaglobulinemia. J. Exp. Med. 187: 71-77, 1998. [PubMed: 9419212] [Full Text: https://doi.org/10.1084/jem.187.1.71]

  2. Moens, L. N., Falk-Sorqvist, E., Asplund, A. C., Bernatowska, E., Smith, C. I. E., Nilsson, M. Diagnostics of primary immunodeficiency diseases: a sequencing capture approach. PLoS One 9: e114901, 2014. Note: Electronic Article. [PubMed: 25502423] [Full Text: https://doi.org/10.1371/journal.pone.0114901]


Contributors:
Joanna S. Amberger - updated : 06/13/2016
Joanna S. Amberger - updated : 8/14/2015

Creation Date:
Cassandra L. Kniffin : 7/26/2010

Edit History:
alopez : 11/15/2022
carol : 06/08/2020
carol : 06/13/2016
joanna : 8/14/2015
carol : 5/1/2013
ckniffin : 5/1/2013
terry : 4/28/2011
terry : 4/27/2011
carol : 8/3/2010
ckniffin : 7/29/2010